156. レット症候群 ［臨床試験数：36，薬物数：49（DrugBank：19），標的遺伝子数：77，標的パスウェイ数：112］
Searched query = "Rett syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
|1||EUCTR2012-005021-76-IT||31/01/2013||11/12/2012||Phase 2A clinical trial conducted on children affected by Rett syndrome and who are casually administered with the experimental treatment, EPI-743, compared versus the se of placebo.||A Phase 2A Randomized, Placebo Controlled Trial of EPI-743 in Children with Rett Syndrome||Rett Syndrome |
MedDRA version: 14.1Level: HLGTClassification code 10021605Term: Inborn errors of metabolismSystem Organ Class: 10027433 - Metabolism and nutrition disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
|Product Name: EPI-743|
Product Code: NA
Other descriptive name: Alpha-tocotrienol quinone
|EDISON PHARMACEUTICALS INC.||NULL||Not Recruiting||Female: yes|