Epi-743    (DrugBank: -)

2 diseases
告示番号疾患名(ページ内リンク)臨床試験数
21ミトコンドリア病1
156レット症候群2

21. ミトコンドリア病 [臨床試験数:23,薬物数:29(DrugBank:28),標的遺伝子数:44,標的パスウェイ数:65
Searched query = "Mitochondrial disease"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 23 trial found
No.TrialIDDate_
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Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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Inclusion_
agemin
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agemax
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PhaseCountries
1NCT01642056September 1, 201214/7/2012EPI-743 for Metabolism or Mitochondrial DisordersTherapeutic Trial of EPI -743 In Patients With Disorders of Energy Utilization or Oxidation-ReductionMitochondrial Disease;Neurology;MyoptahyDrug: EPI-743;Drug: PlaceboNational Human Genome Research Institute (NHGRI)NULLCompleted2 Years11 YearsAll20Phase 1/Phase 2United States

156. レット症候群 [臨床試験数:36,薬物数:49(DrugBank:19),標的遺伝子数:77,標的パスウェイ数:112
Searched query = "Rett syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
2 / 36 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1EUCTR2012-005021-76-IT31/01/201311/12/2012Phase 2A clinical trial conducted on children affected by Rett syndrome and who are casually administered with the experimental treatment, EPI-743, compared versus the se of placebo.A Phase 2A Randomized, Placebo Controlled Trial of EPI-743 in Children with Rett Syndrome Rett Syndrome
MedDRA version: 14.1Level: HLGTClassification code 10021605Term: Inborn errors of metabolismSystem Organ Class: 10027433 - Metabolism and nutrition disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
Product Name: EPI-743
Product Code: NA
Other descriptive name: Alpha-tocotrienol quinone
EDISON PHARMACEUTICALS INC.NULLNot RecruitingFemale: yes
Male: no
Phase 2Italy
2NCT01822249January 201325/3/2013Phase 2 Study of EPI-743 for Treatment of Rett SyndromeA Phase 2A Randomized, Placebo Controlled Trial of EPI-743 in Children With Rett SyndromeRett SyndromeDrug: EPI-743;Drug: PlaceboEdison Pharmaceuticals IncNULLCompletedN/A18 YearsFemale24Phase 2Italy