Other: liver evaluation    (DrugBank: -)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
240フェニルケトン尿症1

240. フェニルケトン尿症 [臨床試験数:125,薬物数:95(DrugBank:11),標的遺伝子数:1,標的パスウェイ数:5
Searched query = "Phenylketonuria", "PKU", "Phenylalanine hydroxylase deficiency", "PAH deficiency", "Tetrahydrobiopterin deficiency", "BH4 deficiency", "BH4 reactive hyper pheemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 125 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT01465100
(ClinicalTrials.gov)
February 202120/10/2011Liver Cell Transplant for PhenylketonuriaHepatocyte Transplantation for PhenylketonuriaPhenylketonuriaRadiation: Preparative Radiation Therapy;Procedure: Hepatocyte Transplant;Drug: Immunosuppression;Other: Liver Evaluation;Behavioral: Neuro-psychological Assessment;Diagnostic Test: Whole body Phe oxidation testing;Procedure: Liver BiopsyIra FoxNULLRecruiting14 Years55 YearsAll10Phase 1;Phase 2United States