DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
240	フェニルケトン尿症	1

告示番号

疾患名（ページ内リンク）

臨床試験数

240

フェニルケトン尿症

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01395394 (ClinicalTrials.gov)	June 2011	23/6/2011	Phenylketonuria, Oxidative Stress, and BH4	The Ability of Kuvan® (Sapropterin Dihydrochloride) to Prevent Meal-induced Lipid Peroxidation and Endothelial Dysfunction in Patients With Phenylketonuria: a Pilot Study	Phenylketonuria	Drug: Kuvan;Other: Meal Challenge	Emory University	NULL	Terminated	10 Years	45 Years	All	12	Phase 2	United States

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT01395394
(ClinicalTrials.gov)

June 2011

23/6/2011

Phenylketonuria, Oxidative Stress, and BH4

The Ability of Kuvan® (Sapropterin Dihydrochloride) to Prevent Meal-induced Lipid Peroxidation and Endothelial Dysfunction in Patients With Phenylketonuria: a Pilot Study

Phenylketonuria

Drug: Kuvan;Other: Meal Challenge

Emory University

NULL

Terminated

10 Years

45 Years

All

Phase 2

United States