DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
274	骨形成不全症	1

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2012-002553-38-ES (EUCTR)	09/08/2013	09/04/2013	Mesenchymal stem cell based therapy for the treatment of osteogenesis imperfecta	Mesenchymal stem cell based therapy for the treatment of osteogenesis imperfecta - TERCELOI	Osteogenesis imperfecta (OI) is a rare genetic disorder with increased bone fragility of varying severity. In the majority of patients the disease is caused by mutations in collagen type I. Severe OI is characterized by osteopenia, frequent fractures, progressive deformity, short stature, loss of mobility, chronic pain and can lead to premature death. At present a cure does not exist.;Therapeutic area: Body processes [G] - Cell Physiological Phenomena [G04]	Product Name: celulas madre mesenquimales troncales adultas alogenicas de médula ósea no expandida Product Code: REF CRUZADA PEI Nº 12-088 INN or Proposed INN: células mesenquimales troncales adultas alogénicas de médula ósea no expandidas Other descriptive name: células mesenquimales troncales adultas alogénicas de médula ósea no expandidas(ref cruzada PEI nº 12-088)	Itziar Astigarraga Aguirre	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes			Spain

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

EUCTR2012-002553-38-ES
(EUCTR)

09/08/2013

09/04/2013

Mesenchymal stem cell based therapy for the treatment of osteogenesis imperfecta

Mesenchymal stem cell based therapy for the treatment of osteogenesis imperfecta - TERCELOI

Osteogenesis imperfecta (OI) is a rare genetic disorder with increased bone fragility of varying severity. In the majority of patients the disease is caused by mutations in collagen type I. Severe OI is characterized by osteopenia, frequent fractures, progressive deformity, short stature, loss of mobility, chronic pain and can lead to premature death. At present a cure does not exist.;Therapeutic area: Body processes [G] - Cell Physiological Phenomena [G04]

Product Name: celulas madre mesenquimales troncales adultas alogenicas de médula ósea no expandida
Product Code: REF CRUZADA PEI Nº 12-088
INN or Proposed INN: células mesenquimales troncales adultas alogénicas de médula ósea no expandidas
Other descriptive name: células mesenquimales troncales adultas alogénicas de médula ósea no expandidas(ref cruzada PEI nº 12-088)

Itziar Astigarraga Aguirre

NULL

Authorised-recruitment may be ongoing or finished

Female: yes
Male: yes

Spain