Sodium phenylbutyrate (napb)    (DrugBank: Phenylbutyrate)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
3脊髄性筋萎縮症1

3. 脊髄性筋萎縮症 [臨床試験数:179,薬物数:102(DrugBank:26),標的遺伝子数:52,標的パスウェイ数:78
Searched query = "Spinal muscular atrophy", "Myelopathic muscular atrophy", "SMA I", "Werdnig-Hoffman disease", "SMA II", "Dubowitz disease", "SMA III", "Kugelberg-Welander disease", "SMA IV"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 179 trial found
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1NCT00528268
(ClinicalTrials.gov)
July 200710/9/2007Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophyProspective Phase I/II Study to Evaluate Effects of Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophySpinal Muscular AtrophyDrug: Sodium phenylbutyrate (NaPB)University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)CompletedN/A6 MonthsAll14Phase 1;Phase 2United States