DDrare: Database of Drug Development for Rare Diseases

Intralipid/heparin (DrugBank: Heparin)

2 diseases

ID	Disease name (Link within this page)	Number of trials
316	Carnitine cycle disorder	1
317	Trifunctional protein deficiency	1

316. Carnitine cycle disorder [ 4 clinical trials, 10 drugs, (DrugBank: 4 drugs), 2 drug target genes, 9 drug target pathways]

Searched query = "Carnitine cycle disorder", "Carnitine palmitoyltransferase I deficiency", "CPT1 deficiency", "Carnitine palmitoyltransferase II deficiency", "CPT2 deficiency", "Carnitine-acylcarnitine translocase deficiency", "CACT deficiency", "Carnitine transporter deficiency", "OCTN-2 deficiency"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 4 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02517307 (ClinicalTrials.gov)	February 2016	2/7/2015	Fatty Acid Oxidation Defects and Insulin Sensitivity	Role of Fatty Acid Oxidation Defects in Insulin Sensitivity	Very Long-chain Acyl-CoA Dehydrogenase Deficiency;Trifunctional Protein Deficiency;Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency;Medium-chain Acyl-CoA Dehydrogenase Deficiency;Normal Volunteers;Carnitine Palmitoyltransferase II Deficiency, Myopathic	Drug: Intralipid/Heparin;Drug: Glycerol/Saline;Drug: Hyperinsulinemic euglycemic clamp	Oregon Health and Science University	NULL	Recruiting	18 Years	N/A	All	50	N/A	United States

317. Trifunctional protein deficiency [ 3 clinical trials, 8 drugs, (DrugBank: 4 drugs), 1 drug target gene, 1 drug target pathway]

Searched query = "Trifunctional protein deficiency"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 3 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02517307 (ClinicalTrials.gov)	February 2016	2/7/2015	Fatty Acid Oxidation Defects and Insulin Sensitivity	Role of Fatty Acid Oxidation Defects in Insulin Sensitivity	Very Long-chain Acyl-CoA Dehydrogenase Deficiency;Trifunctional Protein Deficiency;Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency;Medium-chain Acyl-CoA Dehydrogenase Deficiency;Normal Volunteers;Carnitine Palmitoyltransferase II Deficiency, Myopathic	Drug: Intralipid/Heparin;Drug: Glycerol/Saline;Drug: Hyperinsulinemic euglycemic clamp	Oregon Health and Science University	NULL	Recruiting	18 Years	N/A	All	50	N/A	United States