DDrare: Database of Drug Development for Rare Diseases

Gentamicin infusions twice a week for six months (DrugBank: Gentamicin)

3 diseases

ID	Disease name (Link within this page)	Number of trials
36	Epidermolysis bullosa	0
113	Muscular dystrophy	1
299	Cystic fibrosis	0

36. Epidermolysis bullosa [ 147 clinical trials, 170 drugs, (DrugBank: 40 drugs), 32 drug target genes, 113 drug target pathways]

Searched query = "Epidermolysis bullosa", "EBS", "JEB", "DDEB", "RDEB", "Kindler syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: . Trials are sorted by Date_enrollment from most recent to oldest in the table.

0 / 147 trial found

113. Muscular dystrophy [ 567 clinical trials, 442 drugs, (DrugBank: 93 drugs), 55 drug target genes, 151 drug target pathways]

Searched query = "Muscular dystrophy", "Dystrophinopathies", "Myotilinopathy", "Laminopathy", "Caveolinopathy", "LGMD1C", "Desminopathy", "Sarcoglycanopathy", "α-dystroglycanopathy", "FCMD", "Walker-Warburg syndrome", "Muscle-eye-brain disease", "Myotonic dystrophy", "Integrin α7 deficient CMD", "Rigid spine syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 567 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00451074 (ClinicalTrials.gov)	March 2007	21/3/2007	Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons	A Six Month Randomized, Clinical Trial of Gentamicin in Duchenne Muscular Dystrophy Subjects With Stop Codon Mutations	Duchenne Muscular Dystrophy	Drug: Gentamicin infusions twice a week for six months	Nationwide Children's Hospital	National Institutes of Health (NIH);National Institute of Neurological Disorders and Stroke (NINDS)	Completed	5 Years	20 Years	Male	12	Phase 1	United States

299. Cystic fibrosis [ 1,592 clinical trials, 1,539 drugs, (DrugBank: 255 drugs), 81 drug target genes, 162 drug target pathways]

Searched query = "Cystic fibrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: . Trials are sorted by Date_enrollment from most recent to oldest in the table.

0 / 1,592 trial found