DDrare
Disease
Drug
Target Gene/Pathway
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Drug
Description in Trials
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Showing 1 to 10 of 10 descriptions
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薬物名(臨床試験情報から抽出)
DrugBank
KEGG DRUG
KEGG GENES
KEGG PATHWAY
指定難病告示番号
1
ALGLUCOSIDASE ALFA
(Synonym:
Myozyme
(TN))
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
2
Alglucosidase Alfa (Genetical Recombination)
(Synonym:
Myozyme
(TN))
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
3
Alglucosidase alfa (GZ419829)
(Synonym:
Myozyme
(TN))
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
4
ALGLUCOSIDASE ALFA (
MYOZYME
)
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
5
Alglucosidase alfa (recombinant human acid alpha-glucosidase [rhGAA])
(Synonym:
Myozyme
(TN))
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
6
Alglucosidase alfa GZ419829
(Synonym:
Myozyme
(TN))
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
7
Myozyme
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
8
Myozyme
50 mg powder for concentrate for solution for infusion
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
9
MYOZYME
®
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256
10
Myozyme
® (alglucosidase alfa)
1件:
Alglucosidase alfa
Alglucosidase alfa
(Synonym:
Myozyme
)
1件:
D03207
D03207
(Name:
Myozyme
(TN))
1件:
GAA
GAA
💬
4件:
Galactose metabolism
Galactose metabolism
,
Lysosome
,
Metabolic pathways
,
Starch and sucrose metabolism
💬
1件:
256
256