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Disease
Drug
Target Gene/Pathway
問合せ先
EN
10. シャルコー・マリー・トゥース病
Charcot-Marie-Tooth disease
Clinical trials
/
Disease details
臨床試験数
:
41
/
薬物数
:
46
- (
DrugBank
:
9
) /
標的遺伝子数
:
11
-
標的パスウェイ数
:
15
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agemin
Inclusion_
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1
NCT00484510
(
ClinicalTrials.gov
)
April 2007
8/6/2007
High Dose Ascorbic Acid Treatment of CMT1A
A Randomized, Placebo-controlled, Double Masked 120 Subject Futility Design Clinical Trial of Ascorbic Acid Treatment of Charcot Marie Tooth Disease Type 1A.
A Randomized, Placebo-controlled, Double Masked 120 Subject Futility Design Clinical Trial of Ascorb ...
Charcot-Marie-Tooth Disease, Type Ia
Drug:
Ascorbic acid
(Vitamin C)
;Drug: placebo
Wayne State University
Muscular Dystrophy Association;Charcot-Marie-Tooth Association
Completed
13 Years
70 Years
Both
110
Phase 2/Phase 3
United States