111. 先天性ミオパチー Congenital myopathy Clinical trials / Disease details

臨床試験数 : 10 / 薬物数 : 17 - (DrugBank : 5) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 9

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02362425 (ClinicalTrials.gov)	February 12, 2015	12/2/2015	Antioxidant Therapy in RYR1-Related Congenital Myopathy	Antioxidant Therapy in RYR1-Related Congenital Myopathy	Neuromuscular Disease	Drug: N-acetylcysteine;Drug: Placebo	National Institute of Nursing Research (NINR)	NULL	Completed	7 Years	N/A	All	63	Phase 1/Phase 2	United States