12. 先天性筋無力症候群 Congenital myasthenic syndrome Clinical trials / Disease details

臨床試験数 : 5 / 薬物数 : 7 - (DrugBank : 3) / 標的遺伝子数 : 5 - 標的パスウェイ数 : 13

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03062631 (ClinicalTrials.gov)	July 3, 2017	21/2/2017	Treatment Use of 3,4 Diaminopyridine in Congenital Myasthenia	Treatment Use of 3,4 Diaminopyridine in Congenital Myasthenia	Congenital Myasthenic Syndrome	Drug: 3,4-Diaminopyridine	Ricardo Maselli	Jacobus Pharmaceutical	Available	3 Months	75 Years	All			United States
2	NCT02189720 (ClinicalTrials.gov)	July 2014	5/7/2014	Expanded Access Study Amifampridine Phosphate in Congenital Myasthenic Syndrome (CMS)	An Open-Label, Expanded Access Protocol for Amifampridine Phosphate Treatment in Patients With Conge ...	Congenital Myasthenic Syndrome	Drug: Amifampridine Phosphate	Catalyst Pharmaceuticals, Inc.	NULL	No longer available	2 Years	N/A	All			United States
3	NCT01765140 (ClinicalTrials.gov)	January 2013	6/1/2013	Treatment Use of 3,4-Diaminopyridine	Treatment Use of 3,4-Diaminopyridine in Congenital Myasthenic Syndrome	Myasthenic Syndromes, Congenital	Drug: 3,4-diaminopyridine	Vern C. Juel, M.D.	NULL	No longer available	N/A	N/A	All			United States
4	NCT01203592 (ClinicalTrials.gov)	September 2010	15/9/2010	Efficacy of Albuterol in the Treatment of Congenital Myasthenic Syndromes	Efficacy of Albuterol in the Treatment of Congenital Myasthenic Syndromes	Congenital Myasthenic Syndrome	Drug: Albuterol	Mayo Clinic	NULL	Completed	2 Years	N/A	Both	21	Phase 1	United States
5	NCT00872950 (ClinicalTrials.gov)	June 2001	30/3/2009	3,4-Diaminopyridine Use in Lambert-Eaton Myasthenic Syndrome(LEMS) and Congenital Myasthenic Syndrom ...	Open Label Trial Of 3,4-Diaminopyridine In Lambert-Eaton Myasthenic Syndrome (LEMS) and Congenital M ...	Lambert-Eaton Myasthenic Syndrome;Congenital Myasthenic Syndrome	Drug: 3,4-DIAMINOPYRIDINE	Lahey Clinic	NULL	Active, not recruiting	18 Years	N/A	All	22	N/A	United States

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