158. 結節性硬化症 Tuberous sclerosis Clinical trials / Disease details


臨床試験数 : 112 薬物数 : 71 - (DrugBank : 19) / 標的遺伝子数 : 35 - 標的パスウェイ数 : 118

  
1 trial found
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
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Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
PhaseCountries
1NCT05323734
(ClinicalTrials.gov)
April 1, 202221/3/2022Adjunctive GNX Treatment Compared With Placebo in Children and Adults With TSC-related EpilepsyA Phase 3, Double-blind, Randomized, Placebo-controlled Trial of Adjunctive Ganaxolone (GNX) Treatment in Children and Adults With Tuberous Sclerosis Complex (TSC)-Related Epilepsy (TrustTSC)Tuberous Sclerosis ComplexDrug: Ganaxalone;Drug: PlaceboMarinus PharmaceuticalsNULLRecruiting1 Year65 YearsAll162Phase 3United States;Canada;France;Germany;Israel;Italy;Spain;United Kingdom