18. 脊髄小脳変性症(多系統萎縮症を除く。) Spinocerebellar degeneration Clinical trials / Disease details


臨床試験数 : 76 薬物数 : 98 - (DrugBank : 31) / 標的遺伝子数 : 44 - 標的パスウェイ数 : 65

  
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT05445323
(ClinicalTrials.gov)
August 24, 202223/6/2022Gene Therapy for Cardiomyopathy Associated With Friedreich's AtaxiaA Phase 1/2 Study of the Safety and Efficacy of LX2006 Gene Therapy in Participants With Cardiomyopathy Associated With Friedreich's AtaxiaFriedreich Ataxia;Cardiomyopathy, SecondaryGenetic: Low dose LX2006;Genetic: High Dose LX2006Lexeo TherapeuticsNULLRecruiting18 Years40 YearsAll10Phase 1/Phase 2United States