19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04532047 (ClinicalTrials.gov)	July 1, 2021	19/8/2020	In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases	In Utero Enzyme Replacement Therapy (ERT) for Prenatally Diagnosed Lysosomal Storage Disorders (LSDs ...	MPS I;MPS II;MPS IVA;MPS VI;Mps VII;Gaucher Disease, Type 2;Gaucher Disease, Type 3;Pompe Disease In ...	Drug: Aldurazyme (laronidase)	University of California, San Francisco	Duke University	Recruiting	18 Years	50 Years	Female	10	Phase 1	United States
2	NCT00418821 (ClinicalTrials.gov)	October 22, 2010	3/1/2007	A Study of the Effect of Aldurazyme® (Laronidase) Treatment on Lactation in Female Patients With Muc ...	A Multicenter, Multinational, Open-Label Study of the Effects of Aldurazyme (Laronidase)Treatment on ...	Mucopolysaccharidosis I;Hurler's Syndrome;Hurler-Scheie Syndrome;Scheie	Biological: Aldurazyme (laronidase)	Genzyme, a Sanofi Company	BioMarin/Genzyme LLC	Recruiting	N/A	N/A	Female	2	Phase 4	Italy;United States

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