19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2021-005356-10-NL (EUCTR)	08/04/2022	18/01/2022	A pivotal study of N-Acetyl-L-Leucine on Niemann-Pick disease type C	Effects of N-Acetyl-L-Leucine on Niemann-Pick disease type C (NPC): A Phase III, randomized, placebo ...	Niemann-Pick Disease type C (NPC) MedDRA version: 20.0;Level: SOC;Classification code 10010331;Term: ...	Product Name: N-acetyl-L-leucine Product Code: IB1001 INN or Proposed INN: N-Acetyl-L Leucine Other des ...	IntraBio Ltd	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	53	Phase 3	United States;Czechia;Slovakia;Spain;Australia;Germany;Netherlands;United Kingdom;Switzerland
2	EUCTR2021-005356-10-CZ (EUCTR)		15/07/2022	A pivotal study of N-Acetyl-L-Leucine on Niemann-Pick disease type C	Effects of N-Acetyl-L-Leucine on Niemann-Pick disease type C (NPC): A Phase III, randomized, placebo ...	Niemann-Pick Disease type C (NPC) MedDRA version: 20.0;Level: SOC;Classification code 10010331;Term: ...	Product Name: N-acetyl-L-leucine Product Code: IB1001 INN or Proposed INN: N-Acetyl-L Leucine Other des ...	IntraBio Ltd	NULL	NA			Female: yes Male: yes	53	Phase 3	United States;Czechia;Czech Republic;Slovakia;Australia;Germany;Netherlands;United Kingdom;Switzerla ...

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