20. 副腎白質ジストロフィー Adrenoleukodystrophy Clinical trials / Disease details

臨床試験数 : 61 / 薬物数 : 90 - (DrugBank : 31) / 標的遺伝子数 : 23 - 標的パスウェイ数 : 126

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2018-001145-14-DE (EUCTR)	23/01/2020	27/11/2018	Clinical study to assess the efficacy and safety of gene therapy for the treatment of cerebral adren ...	A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarab ...	Cerebral Adrenoleukodystrophy (CALD) MedDRA version: 20.0;Level: PT;Classification code 10051260;Ter ...	Product Name: Lenti-D Drug Product INN or Proposed INN: elivaldogene autotemcel Other descriptive name ...	bluebird bio, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	35	Phase 3	France;United States;Netherlands;Germany;United Kingdom;Italy

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