240. フェニルケトン尿症 Phenylketonuria Clinical trials / Disease details


臨床試験数 : 143 薬物数 : 90 - (DrugBank : 10) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 5

  
1 trial found
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enrollment
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agemin
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PhaseCountries
1NCT01465100
(ClinicalTrials.gov)
July 202320/10/2011Liver Cell Transplant for PhenylketonuriaHepatocyte Transplantation for PhenylketonuriaPhenylketonuriaRadiation: Preparative Radiation Therapy;Procedure: Hepatocyte Transplant;Drug: Immunosuppression;Other: Liver Evaluation;Behavioral: Neuro-psychological Assessment;Diagnostic Test: Whole body Phe oxidation testing;Procedure: Liver BiopsyIra FoxNULLRecruiting14 Years55 YearsAll10Phase 1/Phase 2United States