244. メープルシロップ尿症 Maple syrup urine disease Clinical trials / Disease details


臨床試験数 : 1 薬物数 : 1 - (DrugBank : 1) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

  
1 trial found
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enrollment
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agemin
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1NCT01529060
(ClinicalTrials.gov)
February 20136/2/2012Phenylbutyrate Therapy for Maple Syrup Urine DiseaseA Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine DiseaseMaple Syrup Urine DiseaseDrug: Phenylbutyrate;Drug: Placebo powderBrendan LeeNULLCompleted3 YearsN/AAll20Phase 2/Phase 3United States