246. メチルマロン酸血症 Methylmalonic acidemia Clinical trials / Disease details

臨床試験数 : 23 / 薬物数 : 31 - (DrugBank : 8) / 標的遺伝子数 : 17 - 標的パスウェイ数 : 23

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	JPRN-jRCT2041210065	04/09/2021	04/09/2021	A Phase I/II Study of Bucladesine in Patients with Severe Methylmalonic Acidemia	A Phase I/II Multi-Institutional Study of Bucladesinein Patients with Severe Methylmalonic Acidemia ...	methylmalonic acidemia;C537358	Bucladesinewill be administered intravenously over 60 minutes once a week. Starting dose is 0.3mg/kg ...	Ito Tetsuya	NULL	Recruiting	>= 3month old	Not applicable	Both	6	Phase 1-2	Japan

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