256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details

臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105

1 trial found

diseases per page:

Showing 1 to 1 of 1 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03533673 (ClinicalTrials.gov)	December 17, 2018	13/4/2018	AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease	A Phase 1 Study of the Safety of AAV2/8-LSPhGAA (ACTUS-101) in Late-onset Pompe Disease	Pompe Disease	Biological: ACTUS-101	Asklepios Biopharmaceutical, Inc.	NULL	Recruiting	18 Years	N/A	All	13	Phase 1/Phase 2	United States