3. 脊髄性筋萎縮症 Spinal muscular atrophy Clinical trials / Disease details
臨床試験数 : 237 / 薬物数 : 123 - (DrugBank : 29) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 75
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | EUCTR2021-006781-21-DK (EUCTR) | 20/12/2022 | Long-term follow-up of patients with spinal muscular atrophy Treated with OAV101 in Clinical Trials | Long-term follow-up of patients with spinal muscular atrophy Treated with OAV101 IT or OAV101 IV in Clinical Trials | Spinal Muscular Atrophy MedDRA version: 20.1;Level: PT;Classification code 10041582;Term: Spinal muscular atrophy;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16] | Trade Name: Zolgensma 2 x 1013 vg (vector genomes)/mL solution for infusion Product Name: OAV101 Product Code: OAV101 Trade Name: Zolgensma 2 x 1013 vg (vector genomes)/mL solution for infusion Product Name: OAV101 Product Code: OAV101 | Novartis Pharma AG | NULL | NA | Female: yes Male: yes | 260 | Phase 4 | United States;Saudi Arabia;Taiwan;Greece;Thailand;Spain;Colombia;Switzerland;Italy;India;France;Malaysia;Viet Nam;Australia;Denmark;South Africa;Netherlands;China;United Kingdom;Egypt;Mexico;Canada;Belgium;Brazil;Singapore;Germany;Japan |