310. 先天異常症候群 Congenital anomalies syndrome Clinical trials / Disease details


臨床試験数 : 11 薬物数 : 20 - (DrugBank : 10) / 標的遺伝子数 : 3 - 標的パスウェイ数 : 7

  
1 trial found
No.TrialIDDate_
enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT00272844
(ClinicalTrials.gov)
January 19984/1/2006Treatment of the Cholesterol Defect in Smith-Lemli-Opitz SyndromeTreatment of the Cholesterol Defect in Smith-Lemli-Opitz SyndromeSmith-Lemli-Opitz SyndromeDrug: crystalline cholesterol oil-based suspensionBoston Children’s HospitalNULLCompletedN/AN/AAll23Phase 1/Phase 2United States