337. ホモシスチン尿症 Homocystinuria Clinical trials / Disease details

臨床試験数 : 16 / 薬物数 : 19 - (DrugBank : 7) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 23

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05154890 (ClinicalTrials.gov)	May 13, 2021	20/8/2021	A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS Deficiency	A Phase 1/2 Multiple Ascending-Dose Study in Subjects With Homocystinuria Due to Cystathionine ß-Syn ...	Homocystinuria Due to Cystathionine Beta-Synthase Deficiency	Drug: Pegtarviliase	Aeglea Biotherapeutics	NULL	Recruiting	12 Years	N/A	All	36	Phase 1/Phase 2	United States;Australia;United Kingdom
2	EUCTR2019-004791-19-GB (EUCTR)	11/05/2020	14/01/2020	A Phase 1/2 Study of ACN00177in Subjects With Homocystinuria Due to Cystathionine ß-Synthase (CBS) D ...	A Phase 1/2 Multiple Ascending-Dose Study in Subjects With Homocystinuria Due to Cystathionine ß-Syn ...	Homocystinuria Due to Cystathionine ß-Synthase (CBS) Deficiency MedDRA version: 20.0;Level: PT;Class ...	Product Code: ACN00177	Aeglea Biotherapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	25	Phase 1	United Kingdom

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