65. 原発性免疫不全症候群 Primary immunodeficiency Clinical trials / Disease details


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217

  
1 trial found
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agemin
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PhaseCountries
1NCT01420627
(ClinicalTrials.gov)
January 24, 201418/8/2011EZN-2279 in Patients With ADA-SCIDA Study of EZN-2279 (Polyethylene Glycol Recombinant Adenosine Deaminase [PEG-rADA]) Administered as a Weekly Intramuscular Injection in Patients With Adenosine Deaminase (ADA)-Deficient Combined ImmunodeficiencyADA-SCID;Adenosine Deaminase Deficiency;Severe Combined ImmunodeficiencyBiological: EZN-2279;Biological: AdagenLeadiant Biosciences, Inc.NULLCompletedN/AN/AAll7Phase 3United States