90. 網膜色素変性症 Retinitis pigmentosa Clinical trials / Disease details
臨床試験数 : 147 / 薬物数 : 176 - (DrugBank : 43) / 標的遺伝子数 : 49 - 標的パスウェイ数 : 110
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04517149 (ClinicalTrials.gov) | June 9, 2020 | 14/8/2020 | 4D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP) | An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR Gene | X-Linked Retinitis Pigmentosa | Biological: 4D-125 IVT Injection;Other: Observational | 4D Molecular Therapeutics | NULL | Active, not recruiting | 12 Years | N/A | Male | 21 | Phase 1/Phase 2 | United States |