90. 網膜色素変性症 Retinitis pigmentosa Clinical trials / Disease details


臨床試験数 : 147 薬物数 : 176 - (DrugBank : 43) / 標的遺伝子数 : 49 - 標的パスウェイ数 : 110

  
1 trial found
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enrollment
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agemin
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1NCT03252847
(ClinicalTrials.gov)
July 14, 20171/8/2017Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2-.RPGR) for Gene Therapy of Adults and Children With X-linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaGenetic: AAV2/5-RPGRMeiraGTx UK II LtdSyne Qua Non Limited;Bionical EmasCompleted5 YearsN/AMale49Phase 1/Phase 2United States;United Kingdom