111. Congenital myopathy Clinical trials / Disease details


Clinical trials : 10 Drugs : 17 - (DrugBank : 5) / Drug target gene : 1 - Drug target pathways : 9

  
1 trial found
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1NCT02362425
(ClinicalTrials.gov)
February 12, 201512/2/2015Antioxidant Therapy in RYR1-Related Congenital MyopathyAntioxidant Therapy in RYR1-Related Congenital MyopathyNeuromuscular DiseaseDrug: N-acetylcysteine;Drug: PlaceboNational Institute of Nursing Research (NINR)NULLCompleted7 YearsN/AAll63Phase 1/Phase 2United States