160. Congenital ichthyosis Clinical trials / Disease details
Clinical trials : 42 / Drugs : 71 - (DrugBank : 21) / Drug target genes : 18 - Drug target pathways : 112
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
1 | NCT01545323 (ClinicalTrials.gov) | April 2014 | 1/3/2012 | Gene Therapy for Netherton Syndrome | Phase I Study of Ex-vivo Lentiviral Gene Therapy for the Inherited Skin Disease Netherton Syndrome | Netherton Syndrome | Genetic: One 20cm2/10cm2 autologous skin sheet graft | Great Ormond Street Hospital for Children NHS Foundation Trust | NULL | Recruiting | N/A | N/A | Both | 5 | Phase 1 | United Kingdom |