65. Primary immunodeficiency Clinical trials / Disease details


Clinical trials : 500 Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217

  
1 trial found
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1NCT04513002
(ClinicalTrials.gov)
March 15, 202226/7/2020Ataxia-telangiectasia: Treating Mitochondrial Dysfunction With a Novel Form of AnaplerosisA Phase 2A/2B Placebo-controlled Randomised Clinical Trial to Test the Ability of Triheptanoin to Protect Primary Airway Epithelial Cells Obtained From Participants With Ataxia-telangiectasia Against Death Induced by Glucose DeprivationAtaxia TelangiectasiaDietary Supplement: TriheptanoinThe University of QueenslandNational Health and Medical Research Council, AustraliaActive, not recruitingN/AN/AAll30Phase 2Australia