HMI-102 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
240フェニルケトン尿症1

240. フェニルケトン尿症


臨床試験数 : 143 薬物数 : 90 - (DrugBank : 10) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 5
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03952156
(ClinicalTrials.gov)
June 10, 20199/5/2019Gene Therapy Clinical Study in Adult PKUA Phase 1/2 Open-Label, Randomized, Concurrently-Controlled, Dose Escalation Study to Evaluate the Safety and Efficacy of HMI-102 in Adult PKU Subjects With PAH DeficiencyPhenylketonurias;PAH DeficiencyGenetic: HMI-102Homology Medicines, IncNULLActive, not recruiting18 Years55 YearsAll28Phase 1/Phase 2United States