Pegvaliase-Pqpz ( DrugBank: Pegvaliase, pegvaliase-pqpz )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
240フェニルケトン尿症1

240. フェニルケトン尿症


臨床試験数 : 143 薬物数 : 90 - (DrugBank : 10) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 5
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT05356377
(ClinicalTrials.gov)
May 25, 202227/4/2022Preliminary Study of Brain Effects of Palynziq-Related Changes in Phenylalanine in Individuals With PKUA Preliminary Study of the Neurological and Neuropsychological Effects of Palynziq-Related Changes in Phenylalanine in Individuals With Phenylketonuria (PKU)PhenylketonuriasDrug: Pegvaliase-PqpzUniversity of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitation18 Years55 YearsAll13United States