ACTUS-101 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
256筋型糖原病1

256. 筋型糖原病


臨床試験数 : 180 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03533673
(ClinicalTrials.gov)
December 17, 201813/4/2018AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe DiseaseA Phase 1 Study of the Safety of AAV2/8-LSPhGAA (ACTUS-101) in Late-onset Pompe DiseasePompe DiseaseBiological: ACTUS-101Asklepios Biopharmaceutical, Inc.NULLRecruiting18 YearsN/AAll13Phase 1/Phase 2United States