Autologous CD34+ cells transduced with WASP lentiviral vector ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群1

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT02333760
(ClinicalTrials.gov)
September 201428/10/2014Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich SyndromeLong Term Safety Follow up of Patients Enrolled in the Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome (GTG002-07 and GTG003-08).Wiskott-Aldrich SyndromeGenetic: Autologous CD34+ cells transduced with WASP lentiviral vectorGenethonNULLActive, not recruitingN/AN/AMale10Phase 1/Phase 2France;United Kingdom