Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene ( DrugBank: - )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
65	原発性免疫不全症候群	2

65. 原発性免疫不全症候群

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臨床試験数 : 500 /  薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01347346 (ClinicalTrials.gov)	May 2011	3/5/2011	Gene Therapy for WAS	Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome	Wiskott-Aldrich Syndrome	Genetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene	Genethon	Hôpital Necker-Enfants Malades	Completed	N/A	N/A	Male	5	Phase 1/Phase 2	France
2	NCT01347242 (ClinicalTrials.gov)	March 2011	3/5/2011	Gene Therapy for Wiskott-Aldrich Syndrome (WAS)	Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome	Wiskott-Aldrich Syndrome	Genetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene	Genethon	Great Ormond Street Hospital for Children NHS Foundation Trust;Institute of Child Health	Completed	N/A	N/A	Male	6	Phase 1/Phase 2	United Kingdom