Ex-vivo gene-therapy ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群1

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT01906541
(ClinicalTrials.gov)
July 201315/7/2013Gene Therapy for X-CGDA Phase I/II Gene Therapy Trial for X-CGD With a SIN Gammaretroviral VectorX-linked Chronic Granulomatous DiseaseGenetic: ex-vivo gene-therapyHubert Serve, Prof., MDNULLRecruiting18 YearsN/ABoth5Phase 1/Phase 2Germany