ETX101 ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
140Dorabe syndrome1

140. Dorabe syndrome


Clinical trials : 116 Drugs : 65 - (DrugBank : 17) / Drug target genes : 50 - Drug target pathways : 64
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enrollment
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registration
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sponsor
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agemin
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agemax
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PhaseCountries
1NCT05419492
(ClinicalTrials.gov)
December 202210/6/2022A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet SyndromeENDEAVOR: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Infants and Children With SCN1A-Positive Dravet SyndromeDravet SyndromeDrug: ETX101Encoded TherapeuticsNULLNot yet recruiting6 Months36 MonthsAll22Phase 1/Phase 2NULL