High Dose LX2006 ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
18Spinocerebellar degeneration1

18. Spinocerebellar degeneration


Clinical trials : 76 Drugs : 98 - (DrugBank : 31) / Drug target genes : 44 - Drug target pathways : 65
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT05445323
(ClinicalTrials.gov)
August 24, 202223/6/2022Gene Therapy for Cardiomyopathy Associated With Friedreich's AtaxiaA Phase 1/2 Study of the Safety and Efficacy of LX2006 Gene Therapy in Participants With Cardiomyopathy Associated With Friedreich's AtaxiaFriedreich Ataxia;Cardiomyopathy, SecondaryGenetic: Low dose LX2006;Genetic: High Dose LX2006Lexeo TherapeuticsNULLRecruiting18 Years40 YearsAll10Phase 1/Phase 2United States