Adrabetadex ( DrugBank: Adrabetadex )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 899 Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182
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enrollment
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registration
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agemin
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PhaseCountries
1NCT03643562
(ClinicalTrials.gov)
June 18, 201819/8/2018Niemann-Pick Type C Treatment With Adrabetadex for Symptoms of Brain and Nervous SystemOpen-label Evaluation of Adrabetadex in Patients With Neurologic Manifestations of Niemann-Pick Type C Disease (NPC)Niemann-Pick Type C DiseaseDrug: AdrabetadexMandos LLCNULLCompleted4 YearsN/AAll27Phase 3United States