Fazisiran Injection ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
231Alpha-1-antitrypsin deficiency1

231. Alpha-1-antitrypsin deficiency


Clinical trials : 93 Drugs : 77 - (DrugBank : 8) / Drug target genes : 10 - Drug target pathways : 36
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
PhaseCountries
1NCT03945292
(ClinicalTrials.gov)
August 7, 20198/5/2019Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT)A Placebo-Controlled, Multi-dose, Phase 2 Study to Determine the Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT) in Patients With Alpha-1 Antitrypsin Deficiency (AATD) [SEQUOIA]Alpha 1-Antitrypsin DeficiencyDrug: Fazisiran Injection;Other: PlaceboArrowhead PharmaceuticalsNULLActive, not recruiting18 Years75 YearsAll40Phase 2United States;Germany;Italy;Netherlands;Portugal;Spain;Canada;Ireland;Sweden