ALGLUCOSIDASE ALFA (MYOZYME) ( DrugBank: Alglucosidase alfa )


1 disease
IDDisease name (Link within this page)Number of trials
256Muscle glycogenosis1

256. Muscle glycogenosis


Clinical trials : 180 Drugs : 133 - (DrugBank : 29) / Drug target genes : 25 - Drug target pathways : 105
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PhaseCountries
1NCT03687333
(ClinicalTrials.gov)
December 4, 201824/9/2018Evaluate Efficacy and Safety in Chinese Patients With Infantile-Onset Pompe Disease With One Year Alglucosidase Alfa TreatmentA Single Arm, Prospective, Open-label, Multi-center Study to Evaluate Efficacy and Safety in Chinese Patients With Infantile-Onset Pompe Disease With One Year Alglucosidase Alfa TreatmentGlycogen Storage Disease Type IIDrug: ALGLUCOSIDASE ALFA (MYOZYME)Genzyme, a Sanofi CompanyNULLCompletedN/A12 MonthsAll10Phase 4China