Antipyretic ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
257Hepatic glycogenosis1

257. Hepatic glycogenosis


Clinical trials : 14 Drugs : 27 - (DrugBank : 7) / Drug target genes : 3 - Drug target pathways : 8
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agemin
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PhaseCountries
1NCT04990388
(ClinicalTrials.gov)
October 18, 202126/7/2021Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III)A Phase 1/2 First-in-human, Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Single Ascending Doses and Repeat Doses of UX053 in Patients With GSD IIIGlycogen Storage Disease Type IIIBiological: UX053;Other: Placebo;Drug: Antipyretic;Drug: H2 Blocker;Drug: H1 BlockerUltragenyx Pharmaceutical IncNULLActive, not recruiting18 YearsN/AAll8Phase 1/Phase 2United States;Canada;France;Italy;Spain;United Kingdom