PTW-002 10 mg/g gel ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
36Epidermolysis bullosa1

36. Epidermolysis bullosa


Clinical trials : 163 Drugs : 185 - (DrugBank : 46) / Drug target genes : 50 - Drug target pathways : 125
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1NCT05529134
(ClinicalTrials.gov)
October 1, 20221/9/2022Study of PTW-002 in Patients With Dominant or Recessive Dystrophic Epidermolysis Bullosa Due to Mutation(s) in Exon 73 of the COL7A1 GeneA Double-blind, Randomized, Intra-patient Placebo- Controlled, Multiple Dose Study of PTW-002 Evaluating Safety, Proof of Mechanism, Preliminary Efficacy, and Systemic Exposure in Patients With Dominant or Recessive Dystrophic Epidermolysis Bullosa (DDEB / RDEB) Due to Mutation(s) in Exon 73 of the COL7A1 GeneDystrophic Epidermolysis BullosaDrug: PTW-002 10 mg/g gel;Drug: PlaceboPhoenicis TherapeuticsNULLNot yet recruiting4 YearsN/AAll8Phase 1/Phase 2United States