1 |
291844 |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
2 |
Ataluren |
Ataluren |
[1] D09323 D09323 💬 |
- |
- |
019 [6] 19, 113, 140, 246, 299, 329 💬 |
3 |
Ataluren 1000mg |
Ataluren |
[1] D09323 D09323 💬 |
- |
- |
246 [1] 246 💬 |
4 |
Ataluren 125mg |
Ataluren |
[1] D09323 D09323 💬 |
- |
- |
246 [1] 246 💬 |
5 |
Ataluren 250mg |
Ataluren |
[1] D09323 D09323 💬 |
- |
- |
246 [1] 246 💬 |
6 |
Carbaglu |
- |
- |
- |
- |
245 [2] 245, 246 💬 |
7 |
Carglumic acid |
Carglumic acid |
[1] D07130 D07130 💬 |
CPS1 [1] CPS1 💬 |
Alanine, aspartate and glutamate metabolism [6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
245 [3] 245, 246, 251 💬 |
8 |
Carglumic acid (carbaglu®) |
Carglumic acid |
[1] D07130 D07130 💬 |
CPS1 [1] CPS1 💬 |
Alanine, aspartate and glutamate metabolism [6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
245 [2] 245, 246 💬 |
9 |
Compound 1a |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
10 |
Hlb-001 |
- |
- |
- |
- |
246 [1] 246 💬 |
11 |
Mrna-3704 |
- |
- |
- |
- |
246 [1] 246 💬 |
12 |
N-carbamylglutamate |
Carglumic acid |
[1] D07130 D07130 💬 |
CPS1 [1] CPS1 💬 |
Alanine, aspartate and glutamate metabolism [6] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
245 [2] 245, 246 💬 |
13 |
Other: standard of care |
- |
- |
- |
- |
013 [7] 13, 49, 64, 85, 96, 245, 246 💬 |
14 |
Ptc-0161480 |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
15 |
Ptc-124 |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
16 |
Ptc-c124 |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
17 |
Ptc124 |
- |
- |
- |
- |
019 [4] 19, 113, 246, 299 💬 |
18 |
Rps 2505 |
- |
- |
- |
- |
246 [2] 246, 299 💬 |
19 |
Standard of care treatment |
- |
- |
- |
- |
245 [2] 245, 246 💬 |