111. Congenital myopathy
7 clinical trials,   13 drugs   (DrugBank: 4 drugs),   1 drug target gene,   8 drug target pathways

Other name(s) = "Nemaline myopathy", "Central core disease", "Minicore myopathy", "Myotubular myopathy", "Centronuclear myopathy", "Congenital fiber-type disproportion myopathy"