241. Hypertyrosinemia type I
14 clinical trials,   7 drugs   (DrugBank: 1 drug),   1 drug target gene,   5 drug target pathways

Other name(s) = "Tyrosinemia type I", "Tyrosinemia I", "Hereditary tyrosinemia, Type I", "Fumarylacetoacetate hydrolase deficiency", "FAH deficiency"