324. Methylglutaconic aciduria
3 clinical trials,   4 drugs   (DrugBank: 3 drugs),   1 drug target gene,   8 drug target pathways

Other name(s) = "3-methylglutaconyl-CoA hydratase deficiency", "3-MGA", "Barth syndrome", "Costeff syndrome", "Mitochondrial respiratory chain disorder", "Dilated cardiomyopathy with ataxia syndrome", "DCMA syndrome"