DDrare: Database of Drug Development for Rare Diseases

1. 球脊髄性筋萎縮症
［臨床試験数：17，薬物数：16（DrugBank：8），標的遺伝子数：10，標的パスウェイ数：15］

Searched query = "Spinal and bulbar muscular atrophy", "Spinobulbar muscular atrophy", "SBMA", "Kennedy disease", "Kennedy-Alter-Sung syndrome"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Drug = Acetate; BVS857; Clenbuterol; Creatine; Dutasteride; Goserelin; Leuprolide; Leuprorelin; Leuprorelin Acetate; MONORES*30CPR 20MCG; Mexiletine; Monores; Procedure: Electrophysiologic study; Procedure: tissue biopsy; TAP-144-SR(3M); Testosterone

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00851461 (ClinicalTrials.gov)	April 2008	25/2/2009	Effect of Goserelin (Zoladex®) in Spinal and Bulbar Muscular Atrophy	Effect of Goserelin (Zoladex®) in Spinal and Bulbar Muscular Atrophy in Thai Patients	Spinobulbar Muscular Atrophy;Kennedy's Disease	Drug: Goserelin;Procedure: Electrophysiologic study;Procedure: tissue biopsy	Ramathibodi Hospital	AstraZeneca	Completed	20 Years	N/A	Male	10	Phase 4	Thailand

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT00851461
(ClinicalTrials.gov)

April 2008

25/2/2009

Effect of Goserelin (Zoladex®) in Spinal and Bulbar Muscular Atrophy

Effect of Goserelin (Zoladex®) in Spinal and Bulbar Muscular Atrophy in Thai Patients

Spinobulbar Muscular Atrophy;Kennedy's Disease

Drug: Goserelin;Procedure: Electrophysiologic study;Procedure: tissue biopsy

Ramathibodi Hospital

AstraZeneca

Completed

20 Years

N/A

Male

Phase 4

Thailand