231. α1-アンチトリプシン欠乏症
[臨床試験数:83,薬物数:89(DrugBank:16),標的遺伝子数:35,標的パスウェイ数:46

Searched query = "Alpha-1-antitrypsin deficiency", "AATD"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

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1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04174118
(ClinicalTrials.gov)
October 24, 20196/11/2019A Study of DCR-A1AT in Healthy Adult Volunteers and Patients With A1ATD-Associated Liver DiseaseA Phase 1/2 Ascending Dose, Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics Study of Subcutaneously Administered DCR-A1AT in Healthy Adult Volunteers and Patients With Alpha1-Antitrypsin-Deficiency-Associated Liver DiseaseAlpha 1-Antitrypsin DeficiencyDrug: DCR-A1AT;Drug: PlaceboDicerna Pharmaceuticals, Inc.NULLRecruiting18 Years70 YearsAll60Phase 1;Phase 2Sweden