244. メープルシロップ尿症
[臨床試験数:1,薬物数:1(DrugBank:1),標的遺伝子数:0,標的パスウェイ数:0]

Searched query = "Maple syrup urine disease", "MSUD"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
PhaseCountries
1NCT01529060
(ClinicalTrials.gov)
February 20136/2/2012Phenylbutyrate Therapy for Maple Syrup Urine DiseaseA Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyrate in the Treatment of Maple Syrup Urine DiseaseMaple Syrup Urine DiseaseDrug: Phenylbutyrate;Drug: Placebo powderBrendan LeeNULLCompleted3 YearsN/AAll20Phase 2;Phase 3United States